Please note that session details are tentative and subject to confirmation from all speakers.
The full program will be released in mid-September.
7:45-8:45am
Join us for an engaging session featuring presentations from Thomas Jaki and Katherine (Kate) Lee.
All are welcome to join this session, though RSVPs are essential. A light breakfast and tea and coffee will be served.
9:00-10:05am
Rory Wolfe Opening address
James Matcham ICH E20: A New Era for Adaptive Designs in Clinical Development
Kert Viele Novel and emerging statistical designs for trials in rare diseases
Moderated Q&A
10:05-11:00am
The Debate: Modern approaches to trials for rare disease have gone too far.
Chair: Tom Snelling
Speaking for the motion:
Liz Ryan
Julie Marsh
Speaking against the motion:
Kristy Robledo
Ian Marschner
11:00-11:25am
11:25am-12:50pm
Details TBA
11:25am-12:50pm
Details TBA
12:50-1:40pm
During the lunch hour, come along to listen to our 5-minute poster presentations in the foyer.
1:40-3:05pm
Details TBA
1:40-3:05pm
Details TBA
3:05-3:30pm
3:30-5:00pm
Chair: Kate Lee and Melissa Middleton
Steve Webb Current limitations of endpoints - how can we do better?
Charlie McLeod Co-designing outcome measures with those with lived experience - a clinician's perspective
Hannah Johns The win ratio: a novel approach for handling complex patient outcomes
Chris Selman Analysing ordinal outcome data with the Bayesian proportional odds model
Thomas Jaki Dose-finding for combination treatments accounting for safety and activity with delayed outcomes
Panel discussion
5:00-6:00pm
All delegates are invited to join us for drinks and canapes in the venue foyer.
The price of the reception is included in your registration. RSVPs are essential when registering.